U.S. flag

An official website of the United States government

Format

Send to:

Choose Destination

Immunodeficiency 121 with autoinflammation(IMD121)

MedGen UID:
1857174
Concept ID:
C5935616
Disease or Syndrome
Synonyms: IMD121; IMMUNODEFICIENCY 121 WITH AUTOINFLAMMATION
 
Gene (location): PSMB10 (16q22.1)
 
Monarch Initiative: MONDO:0971001
OMIM®: 620807

Definition

Immunodeficiency-121 with autoinflammation (IMD121) is a complex immunologic disorder characterized clinically by T-, B-, NK+/- severe combined immunodeficiency (SCID) associated with failure to thrive, erythrodermia, diarrhea, and alopecia. Symptom onset is in early infancy. Laboratory studies show lymphopenia with reduced or absent B cells, decreased T cells, skewed T-cell repertoire, and eosinophilia. Treatment with hematopoietic stem cell transplant (HSCT) is often complicated by severe inflammatory post-transplant complications (van der Made et al., 2024). [from OMIM]

Recent clinical studies

Diagnosis

Dirks J, Wölfl M, Speer CP, Härtel C, Morbach H
Neonatology 2024;121(5):646-655. Epub 2024 Aug 23 doi: 10.1159/000540436. PMID: 39182489

Therapy

Çağdaş D, Sürücü N, Tan Ç, Kayaoğlu B, Özgül RK, Akkaya-Ulum YZ, Aydınoğlu AT, Aytaç S, Gümrük F, Balci-Hayta B, Balci-Peynircioğlu B, Özen S, Gürsel M, Tezcan İ
Mol Immunol 2020 May;121:28-37. Epub 2020 Mar 6 doi: 10.1016/j.molimm.2020.02.014. PMID: 32151906

Supplemental Content

Table of contents

    Clinical resources

    Consumer resources

    Recent activity

    Your browsing activity is empty.

    Activity recording is turned off.

    Turn recording back on

    See more...