Large1 gene transfer in older myd mice with severe muscular dystrophy restores muscle function and greatly improves survival.
Yonekawa T, Rauckhorst AJ, El-Hattab S, Cuellar MA, Venzke D, Anderson ME, Okuma H, Pewa AD, Taylor EB, Campbell KP. Sci Adv. 2022 May 27; 8(21):eabn0379. Epub 2022 May 25.